Experimental gene therapy restores some vision in patients with inherited blindness
·1 min
Experimental Gene-Editing Treatment Shows Promise in Correcting Inherited Blindness #
A young college student, Olivia Cook, who has had limited vision her whole life as a result of an inherited retinal disorder, has undergone an experimental gene-editing treatment that has significantly improved her vision. Cook participated in a clinical trial that utilized the gene-editing tool CRISPR to correct her specific form of inherited blindness. The treatment, which was found to be safe and effective in a Phase 1/2 trial, resulted in meaningful improvements in vision for most participants, with no serious side effects reported. The therapy is still experimental and requires further testing before widespread use.